hemophiliaUpdated:19-03-2025
Sickle Cell Disease is an inherited genetic disorder.
The people who suffer from this disease inherit two sickle hemoglobin genes one from the mother and one from the father.
This leads to the development of crescent or sickle-shaped red blood cells that are sticky and stiff and block the flow of blood through the blood vessels to organs and limbs.
This can damage the organs cause a lot of pain and lead to certain infections.
Symptoms of Sickle Cell Disease
The symptoms vary from mild to severe and in extreme cases require hospitalization of the patients.
Although it is a birth defect, it does not show until the infant is four months old.
Common symptoms include pain and anemia.
Treatment for Sickle Cell Disease
There is no cure for this disorder and only proper care can help improve the quality of life.
But the latest treatment options are also available, consult a physician for details on this.
The patient is referred to a special care team that outlines a complete future medical plan for the child or the adult.
In cases where the patients keep on experiencing pain despite preventive measures, the medication hydroxycarbamide is usually recommended.
Here are some of the latest treatments for Sickle cell disease
Gene Therapies for Sickel Cell Disease
1. Casgevy
2. Lyfgenia
Other Treatment options
1. Voxelotor
2. Crizanlizumab
3. L-glutamine
4. Srem Cell Transplantation
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